Baby Reaches New Heights with Experimental Gene Editing Treatment
A baby boy born with a rare genetic disease is thriving after receiving an experimental gene editing treatment made specifically for him. KJ Muldoon, the nine-and-a-half-month-old from Pennsylvania, was diagnosed shortly after birth with severe CPS1 deficiency, which affects around 1 in a million babies. CPS1 deficiency prevents the body from removing ammonia from the … Read more